Meet Stephanie Harry!
ENERGY IN ACTION - EPISODE 114 The Life and Legacy of Liel Tamar Fenton joins me to share the story of her daughter, Liel....
Meet Dr. Matthew Klein from PTC Therapeutics and learn about navigating clinical trials and COVID-19
Patient-Focused Drug Development (PFDD) meetings are one of the most powerful advocacy tools available to rare disease communities—but most patients have never heard of...