If You Keep the Patient First, You'll Never Go Wrong

ENERGY IN ACTION - EPISODE 094 Barth Syndrome - When the Lack of Fair, Equitable and Appropriate Regulatory Review Process Jeopardizes Ultra-Rare Drug Development  ...

ENERGY IN ACTION - EPISODE 101 The Passionate Life of Josie   Josie van Londen suffers from two interlinked mitochondrial conditions she was diagnosed with...

  ENERGY IN ACTION - EPISODE 038 Patient Led Trials   Steve Smith is a rare disease advocate, father, and a fierce fighter for rare disease...